Disease/ConditionEpilepsy
Seizures
Neurology
Brain and Neurological
Principal InvestigatorAlexis Boro, MD
Trial DescriptionA 5-year Longitudinal Observational Study of Patients Undergoing Therapy for Inflammatory Bowel Disease (TARGET-IBD) -
Click here for more information17-08-399-01
Disease/ConditionInflammatory Bowel Disease
Gastroenterology & Liver Diseases
Colitis and Crohn's Disease
Principal InvestigatorGitit Tomer, MD
Trial DescriptionA 5-year Longitudinal Observational Study of Patients With Nonalcoholic Fatty Liver (NAFL) or Nonalcoholic Steatohepatitis (NASH) -
Click here for more information16-10-402-01
Disease/ConditionLiver Diseases
Gastroenterology & Liver Diseases
Principal InvestigatorBryan Rudolph, MD
Trial DescriptionA Long-Term, Open-Label Follow-up Study of Tofacitinib for Treatment of Juvenile Idiopathic Arthritis (JIA) -
Click here for more information15-10-199-01
Disease/ConditionArthritis
Autoimmune Diseases
Musculoskeletal Diseases
Pediatrics
Rheumatic Diseases
Principal InvestigatorDawn Wahezi, MD
Trial DescriptionA Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs) for Transplantation in Pediatric and Adult Patients With Hematologic Malignancies and Other Indications -
Click here for more information2014-4194
Disease/ConditionAnemia
Hematologic Diseases
Immune System Diseases
Leukemia
Lymphoma
Lymphoproliferative Disorders
Neoplasms
Non-Hodgkins Lymphoma
Oncology (Medical/Hematologic)
Pediatric Hematology/Oncology
Blood Disorders and Diseases
Principal InvestigatorDavid Loeb, MD
Trial DescriptionA Multicenter Safety Study of Unlicensed, Investigational Cryopreserved Cord Blood Units Manufactured by the National Cord Blood Program and Provided for Unrelated Hematopoietic Stem Cell Transplantation of Pediatric and Adult Patients -
Click here for more information2015-5071
Disease/ConditionBlood and Bone Marrow Cancer
Blood Disorders and Diseases
Principal InvestigatorDavid Loeb, MD
Trial DescriptionA Multicenter, Open-label, Randomized, Event-driven Study to Assess Efficacy, Safety and Pharmacokinetics of Macitentan Versus Standard of Care in Children With Pulmonary Arterial Hypertension (PAH) (TOMORROW) -
Click here for more information16-10-366-01
Disease/ConditionHeart and Vascular Diseases
Lung Diseases
Pediatrics
Pulmonary Hypertension
Principal InvestigatorNicole Sutton, MD
Trial DescriptionA Multicenter, Randomized, Double-blind, Placebo-controlled, Parallel-group Study of Ustekinumab in Subjects With Active Systemic Lupus Erythematosus -
Click here for more information18-02-68-01E
Disease/ConditionAutoimmune Diseases
Dermatology
Lupus
Pediatrics
Rheumatic Diseases
Geriatrics
Principal InvestigatorChaim Putterman, MD
Trial DescriptionA Phase 2, Randomized, Double-Blind, Dose-Ranging Study to Determine the Pharmacokinetics, Safety and Tolerability of Vedolizumab IV in Pediatric Subjects With Ulcerative Colitis or Crohn's Disease -
Click here for more information18-10-218-01
Disease/ConditionColitis and Crohn's Disease
Gastroenterology & Liver Diseases
Pediatrics
Inflammatory Bowel Disease
Principal InvestigatorJohn Thompson, MD
Trial DescriptionA Phase 3 Randomized, Double-blind, Placebo-controlled, Multicenter Study to Evaluate the Efficacy and Safety of Pimodivir in Combination With the Standard-of-Care Treatment in Adolescent, Adult, and Elderly Hospitalized Patients w/Influenza A Infection -
Click here for more information17-02-306-01
Disease/ConditionGeriatrics
Infectious Diseases
Influenza
Pediatrics
Principal InvestigatorPaul Riska, MD
Trial DescriptionA Phase 3 Randomized, Placebo-Controlled, Double-Blind Study to Evaluate Upadacitinib in Adolescent and Adult Subjects With Moderate to Severe Atopic Dermatitis -
Click here for more information18-10-220-01
Disease/ConditionDermatology
Pediatrics
Skin Disorders
Geriatrics
Immune System Diseases
Principal InvestigatorHolly Kanavy, MD
Trial DescriptionA Phase 3, Randomized, Open-Label, Multicenter Study to Evaluate the Safety (Compared to Iron Sucrose), Efficacy and Pharmacokinetics of Ferumoxytol for the Treatment of Iron Deficiency Anemia (IDA) in Pediatric Subjects With Chronic Kidney Disease (CKD) -
Click here for more information18-10-59-01
Disease/ConditionHematologic Diseases
Kidney Diseases (incl Chronic Kidney Disease)
Metabolic Diseases
Nephrology
Urologic Diseases
Pediatrics
Principal InvestigatorAnna Zolotnitskaya, MD
Trial DescriptionA Phase II Multi-Center, Randomized, Double-Blind, 24-Week, Parallel Group, Placebo-Controlled Study to Investigate the Efficacy and Safety of Balovaptan (RO5285119) in Children and Adolescents Age 5-17 With Autism Spectrum Disorder (ASD) -
Click here for more information16-10-117-01
Disease/ConditionAutism Spectrum Disorder
Neurodevelopmental Disorders
Pediatrics
Psychiatry - Non Cancer
Mental Health and Disorders
Principal InvestigatorEric Hollander, MD
Trial DescriptionA Phase III Study for Patients With Newly Diagnosed Acute Promyelocytic Leukemia (APL) Using Arsenic Trioxide and All-Trans Retinoic Acid -
Click here for more information2018-9045
Disease/ConditionLeukemia
Oncology (Medical/Hematologic)
Pancreatic Cancer
Pediatric Hematology/Oncology
Neoplasms
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionA Prospective, Observational, Non-Interventional, Post-Marketing, Patient Registry to Collect Data on Routine Clinical Care in Patients Treated With Cholbam®/Kolbam® (Cholic Acid) -
Click here for more information17-08-442-01
Disease/ConditionGastroenterology & Liver Diseases
Pediatrics
Liver Diseases
Principal InvestigatorNadia Ovchinsky, MD
Trial DescriptionA Randomized, Double-Blind, Placebo-Controlled, Multi-Center Pragmatic Clinical Trial To Evaluate The Effectiveness Of Low Dose Oral Methotrexate In Patients With Pediatric Crohn's Disease Initiating Anti-TNF Therapy (COMBINE) -
Click here for more information2017-7692
Disease/ConditionColitis and Crohn's Disease
Gastroenterology & Liver Diseases
Inflammatory Bowel Disease
Pediatrics
Principal InvestigatorGitit Tomer, MD
Trial DescriptionA Study to Compare Bone Marrow Transplantation to Standard Care in Adolescents and Young Adults With Severe Sickle Cell Disease (BMT CTN #1503) -
Click here for more information2016-6694
Disease/ConditionAnemia
Blood Disorders and Diseases
Sickle Cell
Pediatrics
Genetic Disorders
Hematologic Diseases
Principal InvestigatorCaterina Minniti, MD
Trial DescriptionA Trial Comparing Cardiovascular Safety of Degarelix Versus Leuprolide in Patients With Advanced Prostate Cancer and Cardiovascular Disease -
Click here for more information18-06-66Q-01
Disease/ConditionCardiology
Oncology (Medical/Hematologic)
Urogenital Neoplasms
Urologic Oncology (Med Onc)
Prostate Cancer
Principal InvestigatorBenjamin Gartrell, MD
Disease/ConditionBreast Cancer
Neoplasms
Oncology (Medical/Hematologic)
Women`s Health
Principal InvestigatorJoseph Sparano, MD
Trial DescriptionAn Observational, Multicenter Study of the Prevalence of Cerebrotendinous Xanthomatosis (CTX) in Patient Populations Diagnosed With Early-Onset Idiopathic Bilateral Cataracts -
Click here for more information15-10-432-01
Disease/ConditionGenetic Disorders
Ophthalmic Diseases and Disorders
Pediatrics
Principal InvestigatorNorman Medow, MD
Trial DescriptionARCHIVE: A registry for children with vasculitis: e-entry 08-04-111E
Disease/ConditionHeart and Vascular Diseases
Pediatrics
Rheumatic Diseases
Autoimmune Diseases
Principal InvestigatorMaria Yee, MD
Trial DescriptionAssessing the Efficacy of Virtual Reality Analgesia (VRA) in Pediatric Patients for Pain Control During Botox Injections for Spasticity Management: A Randomized Control Trial -
Click here for more information2016-6501
Disease/ConditionAnesthesia and Pain Management
Pediatrics
Rehabilitation Medicine
Principal InvestigatorYuxi Chen, MD
Trial DescriptionAutism Genetics Network, Phase II: Increasing Representation of Human Diversity 2012-537
Disease/ConditionAutism Spectrum Disorder
Neurology
Pediatrics
Genetic Disorders
Principal InvestigatorSophie Molholm, PhD
Trial DescriptionBezlotoxumab (MK-6072) Versus Placebo in Children With Clostridium Difficile Infection (CDI) (MK-6072-001) (MODIFY III) -
Click here for more information17-10-212-01
Disease/ConditionImmune System Diseases
Infectious Diseases
Pediatrics
Principal InvestigatorDavid Goldman, MD
Trial DescriptionBrentuximab Vedotin and Combination Chemotherapy in Treating Younger Patients With Newly Diagnosed Hodgkin Lymphoma -
Click here for more information2015-4877
Disease/ConditionLymphoproliferative Disorders
Neoplasms
Pediatric Hematology/Oncology
Blood and Bone Marrow Cancer
Immune System Diseases
Lymphatic and Spleen Diseases
Lymphoma
Principal InvestigatorLisa Gennarini, MD
Disease/ConditionChild Development
Neurodevelopmental Disorders
Autism Spectrum Disorder
Principal InvestigatorEric Hollander, MD
Disease/ConditionAllergy & Immunology
Allergy and Immune Disorders
Asthma and other Respiratory Diseases
Pediatrics
Principal InvestigatorJonathan Feldman, PhD
Disease/ConditionMedical and Hematologic Oncology
Neuroblastoma
Neoplasms
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionCombination Chemotherapy in Treating Young Patients With Newly Diagnosed High-Risk B Acute Lymphoblastic Leukemia and Ph-Like TKI Sensitive Mutations -
Click here for more information2015-4852
Disease/ConditionBlood and Bone Marrow Cancer
Immune System Diseases
Leukemia
Lymphatic and Spleen Diseases
Lymphoma
Lymphoproliferative Disorders
Neoplasms
Pediatric Hematology/Oncology
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionConsideration of Pedicle Screw Misplacement on a Per-Patient Basis: Can we Better Delineate Surgical Risk? IRB# 12-07-237E
Disease/ConditionBones, Muscles & Joints (Orthopaedics)
Principal InvestigatorVishal Sarwahi, MD
Trial DescriptionDefensin and Innate Mucosal Immune Mediator Expression in Pediatric Inflammatory Bowel Disease 2012-529
Disease/ConditionGastroenterology & Liver Diseases
Inflammatory Bowel Disease
Pediatrics
Principal InvestigatorGitit Tomer, MD
Disease/ConditionDiabetes and Endocrine
Metabolic Diseases
Pediatric Endocrinology
Principal InvestigatorLisa Underland, MD
Trial DescriptionDoes Pedicle Morphology Change with Age? IRB# 11-04-158E
Disease/ConditionBones, Muscles & Joints (Orthopaedics)
Principal InvestigatorVishal Sarwahi, MD
Trial DescriptionEfficacy of a Gluten-free Diet in Difficult to Manage Nephrotic Syndrome: Utility of Plasma Zonulin Levels as a Predictive Biomarker -
Click here for more information2017-8362
Disease/ConditionKidney Diseases (incl Chronic Kidney Disease)
Nephrology
Pediatrics
Urologic Diseases
Principal InvestigatorFrederick Kaskel, MD
Trial DescriptionFollow-up study of children with early diagnosis of autism spectrum disorder IRB# 2007-546
Disease/ConditionAutism Spectrum Disorder
Principal InvestigatorLisa Shulman, MD
Trial DescriptionGene Discoveries in Subjects with Crohns Disease of African Descent IRB# 13-01-024
Disease/Condition -
Principal InvestigatorGitit Tomer, MD
Disease/ConditionAnemia
Hematologic Diseases
Pediatric Hematology/Oncology
Pediatrics
Genetic Disorders
Principal InvestigatorDeepa Manwani, MD
Trial DescriptionIbrutinib in Combination With Corticosteroids Versus Placebo in Combination With Corticosteroids in Subjects With New Onset Chronic Graft Versus Host Disease (cGVHD) (INTEGRATE) -
Click here for more information17-10-17-01
Disease/ConditionGraft Versus Host Disease (GVHD)
Principal InvestigatorOlga Derman, MD
Trial DescriptionInfantile Spasms Multicenter Database IRB# 13-01-027
Disease/ConditionBrain and Neurological
Principal InvestigatorElissa Yozawitz, MD
Disease/ConditionBlood Disorders and Diseases
Principal InvestigatorKerry Morrone, MD
Disease/ConditionBlood Disorders and Diseases
Anesthesia and Pain Management
Principal InvestigatorDeepa Manwani, MD
Trial DescriptionMaintenance Chemotherapy or Observation Following Induction Chemotherapy and Radiation Therapy in Treating Younger Patients With Newly Diagnosed Ependymoma -
Click here for more information10-07-196
Disease/ConditionBrain and Neurological
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionMatched Targeted Therapy (MTT) Recommendation for Patients with Recurrent, Refractory, or High Risk Leukemias -
Click here for more information2016-5971
Disease/ConditionPediatric Hematology/Oncology
Leukemia
Neoplasms
Blood Disorders and Diseases
Cancer
Principal InvestigatorLisa Gennarini, MD
Disease/ConditionSolid Tumor
Principal InvestigatorDaniel Weiser, MD
Disease/ConditionNeonatology
Pediatrics
Overweight, Obesity and Weight Loss
Principal InvestigatorMamta Fuloria, MD
Trial DescriptionMood disorder and cognitive dysfunction in pediatric lupus IRB# 2000-154
Disease/ConditionRheumatic Diseases
Principal InvestigatorChaim Putterman, MD
Trial DescriptionMulticenter Cohort Study To Evaluate Outcomes After Receipt of Targeted Therapy Matched to an Individualized Cancer Therapy (iCat) Recommendations in Children and Young Adults With Solid Tumors: The iCat2, GAIN Consortium Study -
Click here for more information2016-7341
Disease/ConditionCancer
Hematologic Diseases
Pediatric Hematology/Oncology
Solid Tumor
Principal InvestigatorDaniel Weiser, MD
Trial DescriptionMulticenter Prospective Cohort Study on Current Treatments of Legg-Calvé-Perthes Disease (IPSG1) -
Click here for more informationIRB# 2013-2550
Disease/ConditionBones, Muscles & Joints (Orthopaedics)
Principal InvestigatorEric Fornari, MD
Trial DescriptionMulticenter, Open Label, Phase 3 Study of Tabelecleucel for Solid Organ Transplant Subjects With Epstein-Barr Virus-Associated Post-Transplant Lymphoproliferative Disease After Failure of Rituximab or Rituximab and Chemotherapy (ALLELE) -
Click here for more information16-10-296-01
Disease/ConditionEpstein-Barr Virus (EBV)
Lymphoproliferative Disorders
Pediatric Hematology/Oncology
Pediatrics
Solid Organ Transplant (SOT) Complications
Immune System Diseases
Principal InvestigatorDavid Loeb, MD
Trial DescriptionMulticenter, Open-Label, Phase 3 Study of Tabelecleucel for Allogeneic Hematopoietic Cell Transplant Subjects With Epstein-Barr Virus-Associated Post-Transplant Lymphoproliferative Disease After Failure of Rituximab (MATCH Study) -
Click here for more information16-10-211-01
Disease/ConditionEpstein-Barr Virus (EBV)
Immune System Diseases
Lymphatic and Spleen Diseases
Lymphoma
Lymphoproliferative Disorders
Pediatric Hematology/Oncology
Cancer
Principal InvestigatorDavid Loeb, MD
Disease/ConditionDiabetes and Endocrine
Endocrinology
Metabolic Diseases
Autoimmune Diseases
Principal InvestigatorLisa Underland, MD
Disease/ConditionGeriatrics
Kidney Diseases (incl Chronic Kidney Disease)
Nephrotic Syndrome
Pediatrics
Urologic Diseases
Immune System Diseases
Principal InvestigatorFrederick Kaskel, MD
Disease/ConditionSupportive Cancer Care
Principal InvestigatorLisa Gennarini, MD
Disease/ConditionAllergy and Immune Disorders
Principal InvestigatorArye Rubinstein, MD
Trial DescriptionNorth American Pediatric Renal Trials and Collaborative Studies IRB# 02-06-151E
Disease/ConditionKidney Diseases (incl Chronic Kidney Disease)
Principal InvestigatorMarcela Del Rio, MD
Disease/ConditionRheumatic Diseases
Principal InvestigatorYonit Sterba Ruas, MD
Trial DescriptionOpen-label, Phase I/II Study to Evaluate Pharmacokinetics, Pharmacodynamics, Safety, and Anticancer Activity of Avelumab in Pediatric Subjects From Birth to Less Than 18 Years of Age With Refractory or Relapsed Solid Tumors and Lymphoma -
Click here for more information17-10-398Q-01
Disease/ConditionImmune System Diseases
Lymphatic and Spleen Diseases
Lymphoma
Lymphoproliferative Disorders
Neoplasms
Pediatric Hematology/Oncology
Solid Tumor
Principal InvestigatorDavid Loeb, MD
Disease/ConditionKidney Diseases (incl Chronic Kidney Disease)
Principal InvestigatorMamta Fuloria, MD
Trial DescriptionPed Cardiac Quality of LIfe IRB# 08-05-162
Disease/ConditionHeart and Vascular Diseases
Principal InvestigatorJacqueline Lamour, MD
Trial DescriptionPediatric Heart Transplant Study Group IRB# 08-05-166
Disease/ConditionHeart and Vascular Diseases
Principal InvestigatorJacqueline Lamour, MD
Disease/ConditionLung Diseases
Pediatrics
Asthma and other Respiratory Diseases
Principal InvestigatorDeepa Rastogi, MD
Trial DescriptionPersonalized Medicine: Pediatric Total Cancer Care™ Protocol 2013-2690
Disease/ConditionSupportive Cancer Care
Principal InvestigatorDaniel Weiser, MD
Trial DescriptionPharmacodynamic & Safety of Patiromer in Children & Adolescents (2-<18 Yrs) With Chronic Kidney Disease and Hyperkalemia (EMERALD) -
Click here for more information16-10-391-01
Disease/ConditionKidney Diseases (incl Chronic Kidney Disease)
Principal InvestigatorAnna Zolotnitskaya, MD
Trial DescriptionPhase 2 Study: Intranasal Oxytocin vs. Placebo for the Treatment of Hyperphagia in Children and Adolescents With Prader-Willi Syndrome -
Click here for more information2017-8076
Disease/ConditionPsychiatry - Non Cancer
Nervous System Diseases
Child Development
Pediatrics
Genetic Disorders
Principal InvestigatorEric Hollander, MD
Trial DescriptionPhase III Multicenter Open-label Randomized Clinical Trial Comparing Everolimus and Low Dose Tacrolimus to Tacrolimus and Mycophenolate Mofetil at 6 mo Post-Transplant to Prevent Long-term Complications After Pediatric Heart Transplantation -
Click here for more information2017-8626
Disease/ConditionHeart and Vascular Diseases
Kidney Diseases (incl Chronic Kidney Disease)
Pediatrics
Urologic Diseases
Cardiovascular and Thoracic Surgery
Principal InvestigatorJacqueline Lamour, MD
Disease/ConditionCancer and Genetics
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionPromoting Asthma Guidelines and Management through Technology-Based Intervention and Care Coordination (PRAGMATIC) -
Click here for more information2016-6258
Disease/ConditionAsthma and other Respiratory Diseases
Pediatrics
Lung Diseases
Principal InvestigatorMarina Reznik, MD
Trial DescriptionProphylactic Antibiotic Regimens in Tumor Surgery (PARITY): A Multi-Center International Randomized Controlled Trial Comparing Alternative Antibiotic Regimens in Patients Undergoing Tumor Resections With Endoprosthetic Replacements -
Click here for more information2014-4077
Disease/ConditionBone Cancer
Cancer
Infectious Diseases
Musculoskeletal Diseases
Neoplasms
Surgery
Principal InvestigatorDavid Geller, MD
Trial DescriptionProtocol For A Research Database For Hematopoietic Stem Cell Transplantation, Other Cellular Therapies and Marrow Toxic Injuries -
Click here for more information08-05-156E
Disease/ConditionNeoplasms
Oncology (Medical/Hematologic)
Pediatric Hematology/Oncology
Blood and Bone Marrow Cancer
Blood Disorders and Diseases
Hematologic Diseases
Principal InvestigatorIra Braunschweig, MD
Trial DescriptionProtocol for a Research Sample Repository and for a Research Database for Hematopoietic Cell Transplantation, Other Cellular Therapies, and Marrow Toxic Injuries -
Click here for more information2015-5698
Disease/ConditionHematologic Diseases
Neoplasms
Pediatric Hematology/Oncology
Pediatrics
Oncology (Medical/Hematologic)
Principal InvestigatorDavid Loeb, MD
Trial DescriptionProtocol for a Research Sample Repository for Allogeneic Hematopoietic Stem Cell Transplantation -
Click here for more information08-05-155E
Disease/ConditionAutoimmune Diseases
Blood and Bone Marrow Cancer
Blood Disorders and Diseases
Principal InvestigatorIra Braunschweig, MD
Trial DescriptionQuarenta Semanas: Innovative Intervention in Prenatal Care for Reduction of Prematurity (quarenta) -
Click here for more informationIRB# 2014-3022
Disease/ConditionInfant Care
Principal InvestigatorJudy Aschner, MD
Trial DescriptionRadiation Therapy With or Without Combination Chemotherapy or Pazopanib Hydrochloride Before Surgery in Treating Patients With Newly Diagnosed Non-Rhabdomyosarcoma Soft Tissue Sarcomas That Can be Removed by Surgery (PAZNTIS) -
Click here for more information2015-4866
Disease/ConditionSoft Tissue Sarcoma/Cancer
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionResponse and Biology-Based Risk Factor-Guided Therapy in Treating Younger Patients With Non-high Risk Neuroblastoma -
Click here for more informationANBL1232
Disease/ConditionNeuroblastoma
Principal InvestigatorPeter Cole, MD
Disease/ConditionBlood and Bone Marrow Cancer
Principal InvestigatorPeter Cole, MD
Trial DescriptionRisk-Stratified Randomized Phase III Testing of Blinatumomab (NSC#765986) in First Relapse of Childhood B-Lymphoblastic Leukemia (B-ALL) -
Click here for more information2015-4876
Disease/ConditionEpstein-Barr Virus (EBV)
Leukemia
Lymphoma
Lymphoproliferative Disorders
Oncology (Medical/Hematologic)
Neoplasms
Non-Hodgkins Lymphoma
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionSafety Study of Gene Modified Donor T-cells Following TCR Alpha Beta Depleted Stem Cell Transplant -
Click here for more informationIRB# 15-11-347
Disease/ConditionBlood and Bone Marrow Cancer
Principal InvestigatorKris Mahadeo, MD
Trial DescriptionSelf regulation in children with learning disabilities and inattention/hyperactivity IRB# 2006-425
Disease/ConditionChild Development
Principal InvestigatorKatherine Lawson, PhD
Trial DescriptionSensory Integration Therapy in Autism: Mechanisms and Effectiveness IRB# 2014-3795
Disease/ConditionAutism Spectrum Disorder
Principal InvestigatorSophie Molholm, PhD
Disease/ConditionBones, Muscles & Joints (Orthopaedics)
Orthopaedic Surgery
Pediatrics
Neoplasms
Musculoskeletal Diseases
Principal InvestigatorJacob Schulz, MD
Disease/ConditionHematologic Diseases
Pediatrics
Principal InvestigatorDavid Loeb, MD
Disease/ConditionKidney Cancer
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionStudy of the Safety and Effectiveness of SAMSCA® (Tolvaptan) in Children and Adolescents With Euvolemic or Hypervolemic Hyponatremia -
Click here for more informationIRB# 15-08-314
Disease/ConditionHeart and Vascular Diseases
Principal InvestigatorScott Aydin,MD
Trial DescriptionThe Children’s Spine Registry IRB# 2016-6022
Disease/ConditionBones, Muscles & Joints (Orthopaedics)
Principal InvestigatorJaime Gomez, MD
Disease/ConditionBlood and Bone Marrow Cancer
Principal InvestigatorOlga Derman, MD
Trial DescriptionThe Influence of Breakfast on Hormone Responses and Cognitive Performance, as Assessed by CTET in Lean and Obese Adolescent Males -
Click here for more information2015-5542
Disease/ConditionMetabolic Diseases
Pediatric Endocrinology
Overweight, Obesity and Weight Loss
Principal InvestigatorLisa Underland, MD
Trial DescriptionThe National Emergency Airway Registry for Children IRB# 2014-3877
Disease/ConditionAsthma and other Respiratory Diseases
Principal InvestigatorMichael Miksa, MD
Trial DescriptionThe Reliability of X-Ray Based Evaluation of Pedicle Screw Misplacement in Adolescent Spinal Deformity IRB# 11-04-159E
Disease/ConditionBones, Muscles & Joints (Orthopaedics)
Principal InvestigatorVishal Sarwahi, MD
Trial DescriptionThe use of Complementary and Alternative Medicine in Autism IRB# 2007-371
Disease/ConditionAutism Spectrum Disorder
Principal InvestigatorMaria Valicenti-McDermott, MD
Trial DescriptionThe use of Virtual Reality Games to Enhance Therapy for Children with Cerebral Palsy. A pilot Study IRB# 2008-347
Disease/ConditionBrain and Neurological
Principal InvestigatorMaria Valicenti-McDermott, MD
Disease/ConditionLeukemia
Lymphatic and Spleen Diseases
Neoplasms
Pediatric Hematology/Oncology
Lymphoproliferative Disorders
Principal InvestigatorLisa Gennarini, MD
Trial DescriptionUS-based, Observational, Drug Registry of Opsumit® (Macitentan) New Users in Clinical Practice -
Click here for more information14-08-436-01
Disease/ConditionHeart and Vascular Diseases
Principal InvestigatorSandhya Murthy, MD
Trial DescriptionVALENS: A Ph 1/2, Random'd, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate Safety/Preliminary Efficacy of AT342, an AAV8-Delivered Gene Transfer Therapy in Crigler-Najjar Syndrome Subjects Aged 1 Yr and Older -
Click here for more information2017-7918
Disease/ConditionBrain and Neurological
Crigler-Najjar Syndrome
Gastroenterology & Liver Diseases
Heart and Vascular Diseases
Metabolic Diseases
Pediatrics
Principal InvestigatorNadia Ovchinsky, MD
Disease/ConditionAsthma and other Respiratory Diseases
Pediatrics
Lung Diseases
Principal InvestigatorDeepa Rastogi, MD